The US Food and Drug Administration (FDA) approved Panzyga, manufactured by Octapharma AG, for the treatment of PI and ITP in 2018 and for CIDP in adults in 2021. Octapharma commercializes Panzyga ...

The severity of clinical manifestations in CAD can vary depending on the specific type of cold-sensitive antibodies involved. While cold agglutinin and Donath-Landsteiner antibodies recognize antigens ...

Rare Disease Advisor, a trusted source of medical news and feature content for healthcare providers, offers clinicians insight into the latest research to inform clinical practice and improve patient ...

Dan Lier has light chain (AL) amyloidosis—the most common form of amyloidosis. Larry Luxner, senior correspondent for Rare Disease Advisor, interviews former college basketball player Dan Lier, a ...

Overall, 80.9% of patients were in complete remission 1 year after diagnosis irrespective of GPA or MPA cases (79.7% vs 83.8%, respectively). The therapeutic armamentarium for individuals with ...

The overall pooled prevalence of cirrhosis in individuals with homozygous ZZ AATD was 8.17%. Individuals with homozygous ZZ alpha-1 antitrypsin deficiency (AATD) face a substantial burden of liver ...

Results showed a significantly higher prevalence of liver disease among patients with chronic pruritus compared to healthy controls. Patients with liver diseases of different etiologies, including ...

Heather Landau, MD, is an oncologist-hematologist from Sloan Kettering Memorial Cancer Center in New York City, Larry Luxner, senior correspondent for Rare Disease Advisor, interviews ...

Given the multiple genetic mutations typically present in SM-AHN, optimal approaches for SM-AHN remain elusive. A new review article has been published by Dr. Deepti H. Radia, a British clinician who ...

Until more sensitive blood tests are available, bone marrow biopsy is still the gold standard for assessing patients with suspected SM. A new study has determined that even the most sensitive tests ...

91.7% of prognostic studies reported a significant association between bilirubin levels and outcomes. The levels of bilirubin and alkaline phosphatase, as well as composites including these 2, can be ...

Participants who developed certain malignancies such as Richter’s Syndrome and therapy-related myeloid cancers had the poorest prognosis. Individuals with chronic lymphocytic leukemia (CLL) or small ...