Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these ...
Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.
The first person to ever be cured of sickle cell anemia in Louisiana received revolutionary gene therapy. The treatment is ...
Regulators have opened a one-time gene therapy to some of the youngest patients with sickle cell disease. On July 1, 2026, ...
Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to ...
Let’s start with the medical miracle and the man who benefitted from it. His name is Daniel Cressy. He is one of more than ...
The expanded indication lowers the eligible age from 12 to 2 years old for the autologous genome edited gene therapy following successful phase 3 trials in children. The Food and Drug Administration ...